To be the world market leader for enzyme medicines that make a life-changing difference for patients and their families, worldwide.
We view ourselves as an entrepreneurial team of still hungry, still humble innovators and pioneers with a deep sense of urgency/intellectual honesty, taking on some of the toughest, mission-impossible challenges in science and medicine in our quest to develop breakthrough medicines to address critical unmet medical needs. We aim to deliver transformative treatments that target the root causes of these conditions, striving for first-in-class or best-in-class solutions. We are motivated by the commitment to make a life-changing difference for patients and their families. We aim to deliver major value for our partners, our collaborators, our team and our shareholders and to make this world a much better place, free of human suffering and disease.